Long-term natural history in type II and III spinal muscular atrophy: a 4-year international study on the Hammersmith Functional Motor Scale Expanded.

Coratti G;Bovis F;Pera MC;Civitello M;Rohwer A;Salmin F;Glanzman AM;Montes J;Pasternak A;De Sanctis R;Dunaway Young S;Duong T;Mizzoni I;Milev E;Sframeli M;Morando S;Albamonte E;D'Amico A;Catteruccia M;Brolatti N;Pane M;Scoto M;Messina S;Escudero JE;De Waele L;Hirano M;Zolkipli- Cunningham Z;Darras BT;Bertini E;Nascimiento Osorio A;Bruno C;Goemans N;Sansone VA;Day J;Baranello G;Muntoni F;Finkel R;Mercuri E;ISMAC/international SMA consortium.

2024-01-01